Spinal Muscular Atrophy - The disease and its treatments
نویسندگان
چکیده
Less than a decade ago, patients diagnosed with Spinal Muscular Atrophy (SMA) had no treatments other pulmonary, gastrointestinal, and orthopedic care. These palliative were focused on managing symptoms did not address the cause of disease itself. Now, there are several FDA (U.S. Food Drug Administration) approved drugs to treat SMA, which can stop or slow progression. In order discuss development for must first be explained in detail.
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ژورنال
عنوان ژورنال: Archives of community medicine and public health
سال: 2021
ISSN: ['2455-5479']
DOI: https://doi.org/10.17352/2455-5479.000153